Alexion to Explore Challenges in Paediatric Orphan Drug Development

SMi reports (01.07.2016, London, UK): Alexion Associate Director for Regulatory Affairs joins expert speaker line-up at the 5th Orphan Drugs and Rare Diseases event.

London, United Kingdom, July 04, 2016 --( SMi Group’s annual conference on Orphan Drugs and Rare Diseases returns to London for the 5th time on 19th-20th October 2016. Registration is live at

This year’s event will gather a global audience of experts to explore the latest innovations and technologies in orphan drug development and rare disease treatment. In addition, the event provides a platform to discuss recent regulatory updates with a focus on pricing and reimbursement, and emerging markets.

Alexion, one of the world's leading rare disease companies, has joined the expert speaker line-up. Cécile De Coster, Associate Director for Regulatory Affairs, will be giving a keynote address on the challenges associated with paediatric orphan drug development. Some of the important topics she will be covering include complex issues in developing drugs and biological products for rare diseases; how to accelerate the development of therapies for paediatric rare diseases; and methods to overcome the challenges of trial design.

Cécile joins an the speaker panel which includes notable decision-makers from MHRA, NICE, Abeona, Biomarin, Mereo Biopharma, Cell Medica, Tikomed and more.
A complete list of speakers and their topics is available to view on

For those interested in attending Orphan Drugs 2016, there is currently a £200 discount for bookings made by 31 August.

For media enquiries please contact Honey de Gracia on +44(0)207 827 6102 or

5th Orphan Drugs Conference and Exhibition
19-20 October 2016, London UK

For those interested to speak or to exhibit at the event, please contact Alia Malick on +44(0)207 827 6168 or For delegate enquiries, please contact Matt Apps on +44(0)207 827 6093 or

About SMi Group:
Established since 1993, the SMi Group is a global event-production company that specializes in Business-to-Business Conferences, Workshops, Masterclasses and online Communities. We create and deliver events in the Defence, Security, Energy, Utilities, Finance and Pharmaceutical industries. We pride ourselves on having access to the world’s most forward thinking opinion leaders and visionaries, allowing us to bring our communities together to Learn, Engage, Share and Network. More information can be found at
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